Capricor Therapeutics filed a BLA for deramiocel, showing promising results in slowing cardiac dysfunction in DMD ...

I'm fighting a fatal disease that took the life of my brother. I work in biotech and know there are medical advances that ...

A two-day meeting aimed at raising awareness among policymakers and public about rare diseases scheduled for the end of the ...

Pfizer’s decision to halt further marketing of Beqvez is further sign of the sparse patient interest in gene therapies for the bleeding condition.

Wheelchairs 4 Kids, a nonprofit organization dedicated to improving the lives of children with mobility challenges, is ...

Families and doctors spoke out against the cuts at a roundtable at the UMass Chan Medical School in Worcester, Massachusetts.

Telangana's Chief Minister, Revanth Reddy, has intervened to assist Rakesh, a student afflicted with Pseudo Muscular ...

Medically reviewed by Smita Patel, DO Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed ...

Each year, fire departments collect money for the Muscular Dystrophy Association. This year, Galesburg trailed only behind Chicago in Illinois.

Each year, fire departments collect money for the Muscular Dystrophy Association. This year, Galesburg trailed only behind ...