Capricor Therapeutics filed a BLA for deramiocel, showing promising results in slowing cardiac dysfunction in DMD ...

I'm fighting a fatal disease that took the life of my brother. I work in biotech and know there are medical advances that ...

Pfizer’s decision to halt further marketing of Beqvez is further sign of the sparse patient interest in gene therapies for the bleeding condition.

Families and doctors spoke out against the cuts at a roundtable at the UMass Chan Medical School in Worcester, Massachusetts.

Telangana's Chief Minister, Revanth Reddy, has intervened to assist Rakesh, a student afflicted with Pseudo Muscular ...

Medically reviewed by Smita Patel, DO Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed ...

Each year, fire departments collect money for the Muscular Dystrophy Association. This year, Galesburg trailed only behind ...

Reports Q4 revenue $747M, consensus $711.05M. “Our operational transformation and strong financial execution in 2024 is the first step in ...

Solid Biosciences’ gene therapy uses a shortened version of the dystrophin protein, which is engineered to mimic the key functions of full-length dystrophin and allows it be delivered more effectively ...

MILANO - Club Chairman Giuseppe Marotta visited the Centro Clinico NeMO in Milano, the centre of the national network that ...